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thalassemia major

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Bone Denisty Change in Children With Beta Thalassemia Major

Not yet recruiting
  • Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
  • Dexa scan
  • (no location specified)
Sep 29, 2023

Beta-Thalassemia Trial (CS-101 injection)

Not yet recruiting
  • Beta-Thalassemia
  • CS-101 injection
  • (no location specified)
Sep 27, 2023

Thalassemia Major Trial (n-acetylcystine)

Not yet recruiting
  • Thalassemia Major
  • (no location specified)
Mar 9, 2023

ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen Children's Hospital
Feb 24, 2023

Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia, Hemoglobinopathies Trial in San Francisco (in utero hematopoietic

Enrolling by invitation
  • Alpha Thalassemia Major
  • +8 more
  • in utero hematopoietic stem cell transplantation
  • San Francisco, California
    University of California
Oct 28, 2022

"Iron Overload and Endocrinological Diseases"

Recruiting
  • Iron Overload
  • +4 more
    • Modena, Italy
      Unit of Endocrinology of Azienza Ospedaliero-Universitaria di Mo
    Nov 13, 2023

    Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

    Not yet recruiting
    • Thalassemia, Beta
    • Thalassemia Major
    • VGB-Ex01
    • Tianjin, Tianjin, China
      Regenerative Medicine Center
    Sep 11, 2023

    ß Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

    Active, not recruiting
    • β Thalassemia Major
    • γ-globin reactivated autologous hematopoietic stem cells
    • Shanghai, Shanghai, China
      Shanghai Bioray Laboratories Inc.
    Oct 9, 2022

    Beta Thalassemia Major Anemia Trial (SP-420)

    Not yet recruiting
    • Beta Thalassemia Major Anemia
    • (no location specified)
    Jan 20, 2023

    Alpha-Thalassemia, Alpha Thalassemia Major, Alpha Thalassemia Minor Trial in San Francisco

    Recruiting
    • Alpha-Thalassemia
    • +2 more
      • San Francisco, California
        University of California San Francisco
      Oct 7, 2022

      Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

      Not yet recruiting
      • Thalassemia Major
      • γ-globin reactivated autologous hematopoietic stem cells
      • Shanghai, Shanghai, China
        Shanghai Bioray Laboratories Inc
      Jul 1, 2022

      QoL of Pediatric Patients After HSCT and Its Influencing Factors

      Not yet recruiting
      • Thalassemia Major
      • Acute Leukemia
      • Conventional nursing
      • Guangzhou, Guangdong, China
        Sun Yat-sen Memorial Hospital, Sun Yat-sen University
      Sep 4, 2023

      Pulmonary Hypertension (PAH) in Patients With Thalassemia

      Completed
      • Thalassemia Major
      • +2 more
      • Physician standard-of-care according to ESC/ERS Guidelines
      • Orbassano, Turin, Italy
      • +7 more
      Aug 3, 2022

      Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)

      Recruiting
      • Thalassemia Major
      • Transfusion-dependent Anemia
      • Luspatercept Injectable Product
      • Guangzhou, Guangdong, China
        The second affiliated hospital of Sun Yat-sen University
      Jul 15, 2022

      Sickle Cell Disease, Thalassemia Major Trial in Philadelphia (CliniMACS)

      Recruiting
      • Sickle Cell Disease
      • Thalassemia Major
      • CliniMACS
      • Philadelphia, Pennsylvania
        Children's Hospital of Philadelphia
      Dec 22, 2021

      Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)

      Recruiting
      • Transfusion Dependent Beta Thalassemia
      • +3 more
      • EDIT-301
      • Oakland, California
      • +3 more
      Jan 3, 2023

      Beta Thalassemia Major Anemia Trial (blood sampling)

      Not yet recruiting
      • Beta Thalassemia Major Anemia
      • blood sampling
      • (no location specified)
      Jul 5, 2021

      Beta Thalassemia Major Trial in Tirana (Emeramide)

      Completed
      • Beta Thalassemia Major
      • Tirana, Albania
        University Hospital Center "Mother Theresa" Tirana
      Aug 20, 2021

      Different Risk Factors on Growth Parameters of Thalassemic

      Not yet recruiting
      • Thalassemia Major
      • serum ferritin and AST
      • (no location specified)
      Mar 29, 2022

      Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))

      Completed
      • Beta Thalassemia Major
      • Beta Thalassemia Intermedia
      • SOTATERCEPT (ACE-011)
      • Créteil, France
      • +14 more
      Aug 18, 2022

      Leukemia, Myeloid, Acute, Leukemia, B-cell, Leukemia, T Cell Trial in Monza (Sport Therapy)

      Recruiting
      • Leukemia, Myeloid, Acute
      • +7 more
      • Sport Therapy
      • Monza, MB, Italy
        Maria Letizia Verga Center, Pediatric Clinic, University of Mila
      Oct 24, 2022

      Hematologic Diseases Trial in Kunming (BD211 Drug Product)

      Enrolling by invitation
      • Hematologic Diseases
      • BD211 Drug Product
      • Kunming, Yunnan, China
        920th Hospital of Joint Logistics Support Force of People's Libe
      Aug 14, 2021

      Endocrine and Metabolism in Patients With Thalassemia Major

      Recruiting
      • Thalassemia Major
        • Taipei, Taiwan
          Shyang-Rong Shih
        Feb 16, 2021

        Sickle Cell Anemia, Beta-thalassemia Major, Diamond-blackfan Anemia Trial in Pittsburgh (CD3/CD19 depleted leukocytes, CD45RA

        Recruiting
        • Sickle Cell Anemia
        • +2 more
        • CD3/CD19 depleted leukocytes
        • +6 more
        • Pittsburgh, Pennsylvania
          Children's Hospital of Pittsburgh of UPMC
        May 4, 2022

        Thalassemia Major Trial in New York, Bangkok, Chiang Mai (DST-0509, Jadenu, Exjade)

        Completed
        • Thalassemia Major
        • New York, New York
        • +3 more
        Jan 31, 2022